USF Health-TGH team administers first investigational gene therapy for a rare inherited metabolic disorder
The academic medical center is applying cutting-edge science with the hope of reducing or eliminating the cause of PKU, the most common inborn error of metabolism USF Health […]
Nose-to-brain delivery of nanoparticles lowers Huntington’s disease gene expression
USF Health preclinical study tests several formulations of chitosan-enriched siRNA nanoparticles intended to improve gene therapy targeting neurodegenerative diseases Huntington’s disease (HD) is a hereditary brain disease that […]
The end of the beginning: Gene therapy finally comes of age
The age of human gene therapy has at last begun in earnest. This new era presents both tremendous opportunities and hope for our patients, but also brings unprecedented […]
USF gets $2.3M NIH grant to test new Huntington’s disease therapy merging nanomedicine and gene silencing (Audio)
Led by neurologist Dr. Juan-Sanchez-Ramos, the mouse-model study will refine a noninvasive nose-to-brain delivery system using manganese nanoparticles Huntington’s disease (HD) is an incurable, hereditary brain disorder that […]
Symposium highlights new research by industry leaders seeking first treatment for Friedreich’s ataxia [video]
Hosted by FARA and the USF Ataxia Research Center, the annual scientific symposium emphasizes a patient-centered approach to research For the first time in its seven-year history, the […]
Florida Hospital Pepin Heart Institute and USF Health team up for groundbreaking study of new gene therapy for heart failure
The first of its kind, an investigational drug, may enhance the body’s stem cell response at the site of cardiovascular injury TAMPA, Florida (Feb. 20, 2013) – Cardiovascular […]
Healing Hearts
Several clinical trials starting at USF Health’s new Heart Institute this year will offer gene and stem cell therapy approaches to healing damaged hearts Over the past 18 months, […]